Costa poco sponsor perdonato crim negative pompe accumulare Cristo Colpa
Immunological challenges and approaches to immunomodulation in Pompe disease: a literature review. - Abstract - Europe PMC
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Kaplan-Meier curve for overall survival of CRIM-negative IPD patients... | Download Scientific Diagram
Verification of CRIM status classification in patients with IOPD. | Download Table
Frontiers | A Race Against Time—Changing the Natural History of CRIM Negative Infantile Pompe Disease
Enzyme therapy and immune response in relation to CRIM status: the Dutch experience in classic infantile Pompe disease | Journal of Inherited Metabolic Disease
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy | Genetics in Medicine
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Representative Western gel blot showing CRIM negative s | Open-i
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy | Genetics in Medicine
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Therapeutic Options for the Management of Pompe Disease: Current Chall | TCRM
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction - ScienceDirect
Characterization of immune response in Cross-Reactive Immunological Material (CRIM)-positive infantile Pompe disease patients treated with enzyme replacement therapy - ScienceDirect
Algorithm for the Early Diagnosis and Treatment of Patients with Cross Reactive Immunologic Material- Negative Classic Infantile
PDF) Successful Immune Tolerance Induction to Enzyme Replacement Therapy in CRIM-Negative Infantile Pompe Disease
Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
The impact of antibodies on clinical outcomes in diseases treated with therapeutic protein: Lessons learned from infantile Pompe disease | Genetics in Medicine
Pompe Disease
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
CRIM status in PCMCs and fibroblasts, and GAA mutations, in 6 patients... | Download Table
Children | Free Full-Text | The Clinical Management of Pompe Disease: A Pediatric Perspective
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Early ERT Key in Severe Classic Infantile Pompe, Study Finds